Gene therapy is a medical technique that involves altering the genes inside a person’s cells to treat or prevent disease. This approach can involve the addition, removal, or alteration of genetic material within a patient’s cells to correct faulty genes or to provide new functions. Gene therapy aims to address the underlying genetic causes of diseases, particularly genetic disorders and some types of cancer, by directly modifying the genes responsible for the condition. Techniques used in gene therapy may include the delivery of therapeutic genes using vectors, such as viruses, or employing gene editing technologies like CRISPR. The ultimate goal is to restore normal function to affected cells or to enable the body to fight diseases more effectively. Gene therapy holds significant promise for treating a range of conditions, especially those that currently have no cure.
In a remarkable breakthrough for genetic medicine, GEMMA Biotherapeutics has announced an impressive $34 million in seed funding, marking a pivotal moment in the realm of gene therapies. Founded by…